Among individuals with Rett syndrome, treatment with trofinetide was linked to improvements in caregiver-reported outcomes by ...

Rebeca Reyes Diaz, a second-year student at the University of Nevada, Reno Honors College, is a dedicated researcher ...

Learn more about whether ACADIA Pharmaceuticals Inc. or Alvotech is a better investment based on AAII's A+ Investor grades, ...

Scientists have developed a new transgene control system that shows early promise for treating rare brain disorder Rett syndrome.

Neurogene (NGNE) announced a peer-reviewed publication on its EXACT transgene regulation technology. The preclinical ...

About Anavex Life Sciences Corp. Anavex Life Sciences Corp. (Nasdaq: AVXL) is a publicly traded biopharmaceutical company dedicated to the development of novel therapeutics for the treatment of ...

Neurotech International (ASX:NTI) is following in the footsteps of Neuren and targeting Rett Syndrome among other paediatric neurological disorders with its oral cannabinoid drug therapy NTI164. The ...

For example, medications can be used to help regulate menstruation, while lifestyle approaches (like exercise) can help reduce related risks like metabolic syndrome. Work with your healthcare team to ...

Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and families affected by rare neurological diseases, today announced fourth quarter ...

Shares of Sarepta Therapeutics SRPT plunged nearly 24% last week after the company reported the death of a patient following treatment with Elevidys, its one-shot gene therapy for Duchenne ...