Among individuals with Rett syndrome, treatment with trofinetide was linked to improvements in caregiver-reported outcomes by ...

Neurogene has reported encouraging efficacy results with its gene therapy for rare genetic disorder Rett syndrome, but investors' concerns about safety seem to be weighing on its share price.

Neurogene Inc.’s NGNE share price has dipped by 11.19%, which has investors questioning if this is right time to buy.

Rett syndrome is a severe neurodevelopmental disorder of unknown ... until prolonged QTc and associated arrhythmias have been ruled out. The decision regarding treatment for long QTc should then be ...

A gastrostomy tube may be used as an alternate route to supplement nutrition. Gastro-oesophageal reflux may respond to conservative medical treatment with anti-reflux agents, thickened feeds, and ...

Brar's joins forces with Trexo Robotics to provide a transformative gift of two Trexo Robotics gait trainers to clinics ...

Acadia Pharmaceuticals Inc. (Nasdaq: ACAD) today announced that on April 3, 2025, the Compensation Committee of Acadia’s Board of Directors (the "Committee") granted inducement awards consisting of ...

Researchers at Moffitt Cancer Center have found that tapping into the body's own immune system and activating a type of ...

Discover how an emerging technology called tRNA therapy could become the next big thing in genetic disease treatment.

Chronic pain can result from nervous-system overload that creates physical symptoms in response to repressed emotions, therapist Nicole Sachs says.

Genitourinary syndrome of menopause (GSM ... including its causes, symptoms, treatment, and overall outlook for those with this condition. In the years leading up to and including menopause ...